fda-and-biotech News

Sangamo Shares Surge on FDA Fast-Track for Fabry Disease Gene Therapy
FDA & Biotech
2mo ago

Sangamo Shares Surge on FDA Fast-Track for Fabry Disease Gene Therapy

The U.S. regulator's acceptance of a rolling submission for ST-920 could accelerate the approval timeline for the one-time treatment, positioning it against established therapies.

Inhibikase Surges After FDA Allows Key Lung Drug to Skip Phase 2b Trial
FDA & Biotech
2mo ago

Inhibikase Surges After FDA Allows Key Lung Drug to Skip Phase 2b Trial

Company to advance IKT-001 for Pulmonary Arterial Hypertension directly to a pivotal Phase 3 study, accelerating its potential path to market by three years.

Jazz Pharma Executives Sell Stock Into 25% Rally
FDA & Biotech
2mo ago

Jazz Pharma Executives Sell Stock Into 25% Rally

Insider sales totaling over $1.2 million were executed as the company's shares hit a 52-week high following positive oncology drug trial results.

Mesoblast Expands Ryoncil Ambitions with Pivotal Adult GVHD Trial
FDA & Biotech
2mo ago

Mesoblast Expands Ryoncil Ambitions with Pivotal Adult GVHD Trial

Company initiates late-stage study for its cell therapy as a first-line treatment in adults, targeting a larger market beyond its pediatric approval.

Amgen Gains on Full FDA Approval for Lung Cancer Drug Imdelltra
FDA & Biotech
2mo ago

Amgen Gains on Full FDA Approval for Lung Cancer Drug Imdelltra

Pivotal data shows the first-in-class therapy reduced the risk of death by 40%, cementing its role in treating an aggressive form of lung cancer.

AstraZeneca Shares Climb on FDA Nod for Rare Disease Drug Koselugo
FDA & Biotech
2mo ago

AstraZeneca Shares Climb on FDA Nod for Rare Disease Drug Koselugo

The regulator approved an expanded use for the drug to treat adults with a rare genetic disorder, bolstering the company's lucrative rare disease portfolio.

Alumis Insiders Buy Millions in Stock, Signaling Strong Conviction
FDA & Biotech
2mo ago

Alumis Insiders Buy Millions in Stock, Signaling Strong Conviction

Key directors and 10% owners accumulate a significant stake in the biopharma firm, aligning with a bullish Wall Street outlook and a $19 price target.

Alumis Insiders Signal Confidence With Coordinated Stock Purchases
FDA & Biotech
2mo ago

Alumis Insiders Signal Confidence With Coordinated Stock Purchases

Multiple directors at the clinical-stage biopharmaceutical firm have acquired millions in company stock on the open market, signaling strong internal conviction.